The gene editing treatment targets the relatively common 1717-1G>A splicing mutation, which does not respond to many current CF therapies.

The U.S. Food and Drug Administration on Thursday approved the first gene therapy for inherited hearing loss, a one-time ...

First Ascent Biomedical's Functional Precision Oncology bridges that gap by testing living tumor cells to generate actionable data in about 10 days, helping physicians choose the right treatment ...

SYNGAP1 encephalopathy is a rare genetic disorder for which there is no treatment. It causes epilepsy, intellectual ...

Scientists at Memorial Sloan Kettering Cancer Center (MSK) and their colleagues are shedding new light on a tumor's earliest moments - revealing how lung cells with cancer-causing mutations recruit ...

Surprising new research has found that eating a healthy diet packed with fruits, vegetables, and whole grains may lead to a ...

They present a compelling story of radiation, mutation and survival against the odds. But the underlying science didn’t ...

Liquid biopsy enables genomic profiling in prostate cancer with high success rates. Learn more about its potential as a ...

Since emerging from Harvard’s Quantum Computing Lab in 2017, Zapata has led foundational work advancing real-world quantum applications across Fortune 500 enterprises and the public sector, spanning ...

Scientists at Memorial Sloan Kettering Cancer Center (MSK) and their colleagues are shedding new light on a tumor's earliest ...